A rare focus on patients and their families.
Rare diseases and conditions affect 30 million people in the U.S. (1 in 10 Americans) and their families and 350 million people globally. Further, 50 percent of these rare diseases and conditions affect children, making rare diseases and conditions among the most deadly and debilitating disease categories affecting our kids. According to estimates, 95 percent of all rare diseases do not have a single U.S. Food and Drug Administration (FDA) approved drug treatment.
Our goal is to develop and commercialize important and novel products for patients and their families suffering from certain rare neuropsychiatric conditions.